Identification and characterisation of IFNAR1C291* , a rare mutation in familial Parkinsonian disorders

Abstract number
129
Event
European Microscopy Congress 2020
DOI
10.22443/rms.emc2020.129
Corresponding Email
[email protected]
Session
LSA.7 - Pathology, immunocytochemistry and biomolecular labelling
Authors
Mr Lluís Riera Ponsati (1), Dr Emilie Tresse-Gommeaux (1), Dr Shohreh Issazadeh-Navikas (1), Dr Florian Krismer (2), Dr Klaus Seppi (2), Dr Oliver Kretz (4), Dr Alexander Zimprich (3)
Affiliations
1. Biotech Research and Innovation Centre
2. Medical University Innsbruck
3. Medizinische Universität Wien
4. University Medical Center Hamburg-Eppendorf
Keywords

Parkinson's Disease, Neurodegeneration, Neuroimmunology, Type I Interferons

Abstract text

Parkinsonian disorders, including Parkinson’s disease (PD), are the second most common class of neurodegenerative disorders. PD produces a progressive decline in motor and cognitive functions with no cure. Despite numerous efforts, PD is largely sporadic with unknown aetiology (1). Nevertheless, studies of rare familial forms have identified genetic mutations– shedding light on the underlying pathophysiology (2,3,4). Here, we report the identification of a novel, nonsense, disease-linked mutation of the interferon a/b receptor 1 (IFNAR1) gene, p.(C291*), in a family affected by parkinsonian disorders. We found that the p.(C291*) mutation confers loss-of-function and defective neuronal IFNb-IFNAR-signaling, as it encodes for a truncated version of the receptor, with partial deletion of the extracellular domains, transmembrane domain and cytoplasmic tail. IFNAR1C291* expression in primary neurons and had a dominant-negative effect, causing defective neuronal morphology and the pathological hallmarks of PD: accumulation of senesced mitochondria, increased oxidative stress, lowered ATP production, and intracellular inclusions containing phosphorylated a-synuclein, Tau and ubiquitin, as assessed through light and electron microscopyFurthermore, in vivo IFNAR1C291* expression in neurons led to motor and cognitive defects, accompanied by dopamiergic cell lossOur data reveal a new link between innate immunity and Parkinsonian disorders, highlighting new pathogenic mechanisms involved in the aetiology of the disease.


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